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Exploring the frontiers of therapeutic exon skipping for Duchenne muscular dystrophy by double targeting within one or multiple exons. |
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| Authors: | Annemieke Aartsma-Rus Wendy E Kaman Rudie Weij Johan T den Dunnen Gert-Jan B van Ommen Judith C T van Deutekom |
| Affiliation: | DMD Genetic Therapy Group, Center for Human and Clinical Genetics, Leiden University Medical Center, RC Leiden, The Netherlands. |
| Abstract: | |
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