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In vivo T-cell dynamics during immune reconstitution after hematopoietic stem cell gene therapy in adenosine deaminase severe combined immune deficiency
Authors:Selleri Silvia  Brigida Immacolata  Casiraghi Miriam  Scaramuzza Samantha  Cappelli Barbara  Cassani Barbara  Ferrua Francesca  Aker Memet  Slavin Shimon  Scarselli Alessia  Cancrini Caterina  Marktel Sarah  Grazia Roncarolo Maria  Aiuti Alessandro
Affiliation:a San Raffaele Telethon Institute for Gene Therapy, Milan, Italy
b Pediatric Immunohematology and Bone Marrow Transplantation Unit, San Raffaele Scientific Institute, Milan, Italy
c Istituto Clinico Humanitas, Milan, Italy
d University of Rome “Tor Vergata,” Rome, Italy
e Department of Pediatrics, University of Rome “Tor Vergata,” Children’s Hospital Bambino Gesù, Rome, Italy
f Hadassah University Hospital, Jerusalem, Israel
Abstract:
Keywords:Gene therapy   ADA-SCID   senescence   cell cycle   immune reconstitution
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