Affiliation: | a San Raffaele Telethon Institute for Gene Therapy, Milan, Italy b Pediatric Immunohematology and Bone Marrow Transplantation Unit, San Raffaele Scientific Institute, Milan, Italy c Istituto Clinico Humanitas, Milan, Italy d University of Rome “Tor Vergata,” Rome, Italy e Department of Pediatrics, University of Rome “Tor Vergata,” Children’s Hospital Bambino Gesù, Rome, Italy f Hadassah University Hospital, Jerusalem, Israel |