Affiliation: | 1. Department of Intestinal Failure and Liver Diseases, Rigshospitalet, Copenhagen, Denmark;2. Shire Human Genetic Therapies, Inc, a Takeda company, Cambridge, Massachusetts, USA;3. ICON plc, Gaithersburg, Maryland, USA;4. ICON plc, San Francisco, California, USA Institute for Clinical Research and Health Policy Studies, Tufts Medical Center, Boston, Massachusetts, USA;5. Takeda Development Center Americas, Inc, Cambridge, Massachusetts, USA |