Affiliation: | 1. University of Utah, Salt Lake City, UT, USA;2. Oregon Health & Sciences University, Portland, OR, USA;3. Ann and Robert H Lurie Children''s Hospital and Northwestern University Feinberg School of Medicine, Chicago, IL, USA;4. Washington University School of Medicine, St Louis, MO, USA;5. University of Pittsburgh School of Medicine, PA, USA;6. Mount Sinai School of Medicine, New York, NY, USA;g University of Wisconsin, Madison, WI, USA;h BioMarin Pharmaceutical, Novato, CA, USA |