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One-year results of the placebo-controlled ASCEND trial of olipudase alfa enzyme replacement therapy in adults with chronic acid sphingomyelinase deficiency |
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| Authors: | Melissa Wasserstein Laila Arash-Kaps Antonio Barbato Renata Gallagher Roberto Giugliani Norberto Guelbert Carla Hollak Takayuki Ikezoe Robin Lachmann Olivier Lidove Paulina Mabe Eugen Mengel Maurizio Scarpa Ebubekir Senates Michel Tchan Jesus Villarrubia Yixin Chen Maria Iram Awan Monica Kumar |
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