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Systemic Administration of a Recombinant AAV1 Vector Encoding IGF-1 Improves Disease Manifestations in SMA Mice
Authors:Li-Kai Tsai  Chien-Lin Chen  Chen-Hung Ting  Sue Lin-Chao  Wuh-Liang Hwu  James C Dodge  Marco A Passini  Seng H Cheng
Institution:1Department of Neurology, National Taiwan University Hospital and National Taiwan University College of Medicine, Taipei, Taiwan;2Institute of Molecular Biology, Academia Sinica, Taipei, Taiwan;3Department of Medical Genetics, National Taiwan University Hospital, Taipei, Taiwan;4Genzyme, a Sanofi Company, Framingham, Massachusetts, USA
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