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Recombinant factor XIII prophylaxis is safe and effective in young children with congenital factor XIII‐A deficiency: international phase 3b trial results
Authors:B A Kerlin  A Inbal  A Will  M Williams  M‐L Garly  L Jacobsen  S L Kearney
Institution:1. Nationwide Children's Hospital and The Ohio State University College of Medicine, Columbus, OH, USA;2. Thrombosis and Hemostasis Unit, Hematology Department, Rabin Medical Center, Petah Tikva and Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel;3. Royal Manchester Children's Hospital, Manchester, UK;4. Birmingham Children's Hospital, Birmingham, UK;5. Novo Nordisk A/S, S?borg, Denmark;6. Pediatric Hematology/Oncology, Children's Hospitals and Clinics of Minnesota, Minneapolis, MN, USA
Abstract:
Keywords:factor   XIII  factor   XIII deficiency  fibrinolysis  prophylaxis  recombinant factor   XIII‐A subunit
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