|
|||||
|
|
Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery |
|
| Authors: | Catherine Cukras Henry E. Wiley Brett G. Jeffrey H. Nida Sen Amy Turriff Yong Zeng Camasamudram Vijayasarathy Dario Marangoni Lucia Ziccardi Sten Kjellstrom Tae Kwon Park Suja Hiriyanna J. Fraser Wright Peter Colosi Zhijian Wu Ronald A. Bush Lisa L. Wei Paul A. Sieving |
| Affiliation: | 1. NIH, National Eye Institute, Bethesda, MD 20892, USA;2. STRRMD/NIDCD/NIH, Bethesda, MD 20874, USA;3. Neurophysiology of Vision and Neuropathmology Unit, IRCCS Fondazione G.B. Bietti, Rome 00198, Italy;4. Department of Ophthalmology, Lund University, Lund, Sweden;5. Ophthalomology, Soonchunhyang University Bucheon Hospital, Seoul, Korea;6. Ocular Gene Therapy Core, National Eye Institute, Bethesda, MD 20892, USA;7. Ophthalomology, Children’s Hospital of Philadelphia, Philadelphia, PA, USA |
| Abstract: | |
| Keywords: | gene therapy X-linked retinoschisis clinical trial AAV vector ocular disease retinal disease |
| 本文献已被 ScienceDirect 等数据库收录！ | |