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Fabry Registry Data Indicate that Early Initiation of Agalsidase Beta Treatment is Associated with Fewer Clinical Events
Authors:Robert Hopkin  Michael Mauer  Roberta Lemay  Jörg Strotmann  Katherine Sims
Affiliation:1. Department of Internal Medicine, Division of Endocrinology and Metabolism, Academic Medical Centre, Amsterdam, The Netherlands;2. Department of Paediatrics, Academic Medical Centre, Amsterdam, The Netherlands;1. Department of Medical Genetics, Faculty of Medical Sciences, State University of Campinas, Tessália Vieira de Camargo, 126, Barão Geraldo, Cidade Universitária Zeferino Vaz, 13083-887 Campinas, São Paulo, Brazil;2. Department of Pediatrics, Faculty of Medical Sciences, State University of Campinas, Tessália Vieira de Camargo, 126, Barão Geraldo, Cidade Universitária Zeferino Vaz, 13083-887 Campinas, São Paulo, Brazil;3. Laboratory of Pulmonary Physiology, Center for Pediatrics Investigation, Faculty of Medical Sciences, State University of Campinas, Tessália Vieira de Camargo, 126, Barão Geraldo, Cidade Universitária Zeferino Vaz, 13083-887 Campinas, São Paulo, Brazil;1. Medical Genetics Service, HCPA and Department of Genetics, UFRGS, Rua Ramiro Barcelos 2350, Porto Alegre 90035-903, RS, Brazil;2. Independent Medical Consultant. Retired from Salford Royal NHS Foundation Trust October 2011;3. University of Versailles - St Quentin en Yvelines, Division of Medical Genetics, Hôpital Raymond Poincaré (AP-HP), 104 Boulevard Raymond Poincaré, 92380, Garches, France;4. Royal Melbourne Hospital, Department of Nephrology, 6 South West, Grattan Street, Parkville, Vic 3050, Australia;5. Université de Montréal, Hôpital du Sacré-Coeur de Montréal, 5400 Boulevard Gouin Ouest, Montréal (Quebec), Canada H4J 1C5;6. Amicus Therapeutics, 1 Cedar Brook Drive, Cranbury, NJ 08512, USA;1. Unita''Operativa Complessa Ematologia II, A.O.R. Villa Sofia–V. Cervello, Palermo, Italy;2. Dipartimento di Scienze Economiche, Aziendali e Statistiche, Università di Palermo, Palermo, Italy;3. Division of Hematology/Cardeza Foundation, Department of Medicine, Jefferson Medical College, Thomas Jefferson University, Philadelphia, PA, USA;4. Center of Excellence in Sickle Cell Disease, Department of Pediatrics, Pathology and Laboratory Medicine, Boston Medical Center, Boston, MA, USA;5. Department of Hematology, The Royal London Hospital, London, United Kingdom
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