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Elexacaftor/tezacaftor/ivacaftor-real-world clinical effectiveness and safety. A single-center Portuguese study
Authors:Kelly Lopes,Catarina Custó  dio,Carlos Lopes,Raquel Bolas,Pilar Azevedo
Affiliation:1.. Centro Hospitalar Barreiro Montijo EPE, Barreiro, Portugal.; 2.. Hospital Beatriz Ângelo, Loures, Portugal.; 3.. Hospital de Santa Maria, Centro Hospitalar Lisboa Norte EPE, Lisboa, Portugal.; 4.. Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal.
Abstract:
Keywords:Cystic fibrosis   Cystic fibrosis transmembrane conductance regulator   Membrane transport modulators   Treatment outcome
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