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Cationic PMMA Nanoparticles Bind and Deliver Antisense Oligoribonucleotides Allowing Restoration of Dystrophin Expression in the mdx Mouse
Authors:Paola Rimessi   Patrizia Sabatelli   Marina Fabris   Paola Braghetta   Elena Bassi   Pietro Spitali   Gaetano Vattemi   Giuliano Tomelleri   Lara Mari   Daniela Perrone   Alessandro Medici   Marcella Neri   Matteo Bovolenta   Elena Martoni   Nadir M. Maraldi   Francesca Gualandi   Luciano Merlini   Marco Ballestri   Luisa Tondelli   Katia Sparnacci   Paolo Bonaldo   Antonella Caputo   Michele Laus     Alessandra Ferlini
Affiliation:1. Department of Experimental and Diagnostic Medicine, Section of Medical Genetics, University of Ferrara, Ferrara, Italy;2. IGM-CNR, Unit of Bologna c/o IOR, Bologna, Italy;3. Department of Histology, Microbiology, and Medical Biotechnology; University of Padova, Padova, Italy;4. Department of Neurological Sciences and Vision, Section of Clinical Neurology, University of Verona, Verona, Italy;5. Department of Chemistry, University of Ferrara, Ferrara, Italy;6. Department of Biology and Evolution, University of Ferrara, Ferrara, Italy;7. Department of Human Anatomical Sciences, University of Bologna and Laboratory of Cell Biology, IOR, Bologna, Italy;8. ISOF, Consiglio Nazionale delle Ricerche, Bologna, Italy;9. Department of Environmental and Life Sciences INSTM, University of Piemonte Orientale, Alessandria, Italy
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