Affiliation: | 1. Kennedy Krieger Institute, 1741 Ashland Avenue, Baltimore, MD 21205, USA;2. Johns Hopkins University School of Medicine, 733 North Broadway, Baltimore, MD 21205, USA;3. Kennedy Krieger Institute, Johns Hopkins School of Medicine, 707 North Broadway Street, Baltimore, MD 21209, USA;4. Johns Hopkins Hospital, 1800 Orleans Street, Baltimore, MD 21287, USA;1. Janssen Research & Development, LLC, 1125 Trenton Harbouron Road, Titusville, NJ 08560, USA;2. Kaerus Bioscience Ltd, London, UK |