Institution: | 1. Pediatric Hematology, University of North Carolina at Chapel Hill, , Chapel Hill, NC, USA;2. Department of Pediatrics, Siriraj Hospital, Mahidol University, , Bangkok, Thailand;3. Gene Therapy Center, University of North Carolina at Chapel Hill, , Chapel Hill, NC, USA;4. North Carolina Translational and Clinical Sciences Institute, University of North Carolina at Chapel Hill, , Chapel Hill, NC, USA;5. Departments of Biomedical Engineering and Radiation Oncology, University of North Carolina at Chapel Hill, , Chapel Hill, NC, USA;6. Department of Product Research, Fuji‐Gotemba Research Laboratories, Chugai Pharmaceutical Co. Ltd, , Shizuoka, Japan |