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Bone Marrow Transplantation for Inherited Bone Marrow Failure Syndromes
Authors:Parinda Mehta  Franco Locatelli  Jan Stary  Franklin O. Smith
Affiliation:a Cincinnati Children's Hospital Medical Center and the University of Cincinnati College of Medicine, 3333 Burnet Avenue, Cincinnati, OH 45229, USA
b University of Pavia, Ospedale Pediatrico Bambino Gesu, Roma, Italy
c Pediatric Haematology/Oncology Fondazione, IRCCS Policlinico San Matteo, 27100-I, Pavia, Italy
d Department of Pediatrics Hematology and Oncology, University Hospital Motol, Vúvalu 84, 150 06, Prague 5, Czech Republic
Abstract:
Keywords:Inherited bone marrow failure syndromes   Bone marrow transplantation   Gene mutation   Diagnostic tests
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