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CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa Patient
Authors:Daniela Benati  Francesca Miselli  Fabienne Cocchiarella  Clarissa Patrizi  Marta Carretero  Samantha Baldassarri  Virginia Ammendola  Cristina Has  Stefano Colloca  Marcela Del Rio  Fernando Larcher  Alessandra Recchia
Affiliation:1. Centre for Regenerative Medicine, Department of Life Sciences, University of Modena and Reggio Emilia, Modena, Italy;2. Epithelial Biomedicine Division, CIEMAT-CIBERER (Centre for Biomedical Research on Rare Diseases), Madrid, Spain;3. Department of Bioengineering, Universidad Carlos III de Madrid, Madrid, Spain;4. Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz, Madrid, Spain;5. Reithera s.r.l., Rome, Italy;6. Department of Dermatology and Venereology, Faculty of Medicine, University Medical Center Freiburg, Freiburg, Germany
Abstract:
Keywords:CRISPR/Cas9 gene editing  LAMB3 mutations  adhesion advantage
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