| Affiliation: | 1. Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA;2. The Research Institute at Nationwide Children’s Hospital, Columbus, OH 43205, USA;3. The Mannheimer Foundation, Inc., Homestead, FL 33034, USA;4. Department of Biochemistry, School of Biomedical Sciences, Brain Health Research Centre, University of Otago, Dunedin 9016, New Zealand;5. Division of Biology, Kansas State University, Manhattan, KS 66506, USA;6. AveXis Inc., Bannockburn, IL 60015, USA;7. Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD 57069, USA |
