Affiliation: | 1. Unit of Rare Diseases, Department of Pediatrics, Gaslini Institute, , Genoa, Italy;2. Department of Translational Medicine, Section of Pediatrics, Federico II University, , Naples, Italy;3. Division of Metabolism, Department of Pediatric Medicine, “Bambino Gesù” Children's Hospital, IRCCS, , Rome, Italy;4. Hematology, Department of Cellular Biotechnologies and Hematology, “Sapienza” University, , Rome, Italy;5. Giannina Gaslini Institute, , Genova, Italy;6. Department of Pediatrics, University of Bologna, , Bologna, Italy |