Affiliation: | 1. Center for Sickle Cell Disease, University of Tennessee Health Scienter Center, Memphis, Tennessee, USA;2. Division of Hematology and Blood Research Center, University of North Carolina, Chapel Hill, North Carolina, USA;3. Department of Biostatistics, University of North Carolina, Chapel Hill, North Carolina, USA;4. Vanguard Therapeutics, Inc., Half Moon Bay, California, USA |