| Institution: | 1. Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, USA;2. Division of Hematology and Raymond G. Perelman Center for Cellular and Molecular Therapeutics, Children’s Hospital of Philadelphia, Philadelphia, PA, USA;3. Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA;4. Gene & Stem Cell Therapy Program, Centenary Institute, and Faculty of Medicine and Health, The University of Sydney, Sydney, Australia;5. Cell and Molecular Therapies, Royal Prince Alfred Hospital, Camperdown, NSW, Australia;6. Division of Hematology, The Children’s Hospital of Philadelphia, Philadelphia, PA, USA;7. Department of Internal Medicine, Faculty of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil;8. IHTC Hemophilia Unit Cláudio Luiz Pizzigatti Corrêa, INCT do Sangue Hemocentro UNICAMP, University of Campinas, Campinas, São Paulo, Brazil;9. Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, USA;10. Spark Therapeutics, Philadelphia, PA, USA |
