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Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by morpholino antisense oligonucleotides
Authors:Vetrini Francesco  Tammaro Roberta  Bondanza Sergio  Surace Enrico M  Auricchio Alberto  De Luca Michele  Ballabio Andrea  Marigo Valeria
Affiliation:Telethon Institute of Genetics and Medicine (TIGEM), Naples, Italy.
Abstract:
Keywords:albinism  splicing  exon skipping  morpholino oligonucleotide  ocular albinism type 1  OA1  GPR143
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