Affiliation: | 1. Departments of Ophthalmology and Neuroscience, Johns Hopkins University School of Medicine, Baltimore, MD, USA;2. Departments of Medicine and Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, PA, USA;3. REGENXBIO Inc., Rockville, MD, USA;4. Johns Hopkins Biostatistics Center, Department of Biostatistics, Johns Hopkins Bloomberg School of Public Health, Baltimore, MD, USA |