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Allele-specific Col1a1 silencing reduces mutant collagen in fibroblasts from Brtl mouse,a model for classical osteogenesis imperfecta
Authors:Julie Rousseau  Roberta Gioia  Pierre Layrolle  Blandine Lieubeau  Dominique Heymann  Antonio Rossi  Joan C Marini  Valerie Trichet  Antonella Forlino
Abstract:
Keywords:allele-specific Col1a1 silencing  siRNA  shRNA  osteogenesis imperfecta  lentiviral vector
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