Affiliation: | 1. University of Cambridge, Addenbrooke''s Hospital, Cambridge, United Kingdom;2. Northwestern University Feinberg School of Medicine, Ann and Robert H. Lurie Children''s Hospital of Chicago, Chicago, IL, United States;3. National Research Center for Hematology, Moscow, Russian Federation;4. Yale University School of Medicine, New Haven, CT, United States;5. General Hospital of Athens “G. Gennimatas”, Athens, Greece;6. Sanofi Genzyme, Cambridge, MA, United States |